Aim When selecting treatments for type 2 diabetes (T2D), it is important to consider not only
efficacy and safety, but also other treatment attributes that have an impact on patient …

Paroxysmal nocturnal hemoglobinuria (PNH) is a rare, chronic, acquired, hematologic, life-threatening
disease characterized by thrombosis, impaired bone marrow function, and …

Background Asthma control is often overestimated in routine practice, and despite advances
in the understanding of immunopathology and the availability of new precision therapies, …

Introduction Alopecia areata (AA) is an autoimmune disease characterized by hair loss.
Patients with AA experience a range of social and emotional impacts, and the lack of effective …

The Living with Idiopathic Pulmonary Fibrosis (L-IPF) questionnaire was developed with
substantial input from patients with idiopathic pulmonary fibrosis (IPF) to assess symptoms and …

Background Classic congenital adrenal hyperplasia (CAH) due to 21-hydroxylase deficiency
is a rare autosomal recessive condition characterized by cortisol deficiency and excess …

Purpose Previous research suggests that treatment process can have an influence on
patient preference and health state utilities. This study examined preferences and estimated …

Although asthma control is defined by impairment and risk, many control tools only assess 58
symptoms. Confirmatory cross-sectional performance metrics demonstrate that the AIRQ, a …

Objective The objective of this study was to ascertain to what extent adults with migraine
value an early onset of efficacy for preventive migraine treatments. Background In placebo‐…

Purpose Critical asthma outcomes highlighted in clinical guidelines include asthma-related
quality of life, asthma exacerbations, and asthma control. An easy-to-implement measure of …