Cell Stem Cell
Volume 26, Issue 4, 2 April 2020, Pages 503-510.e7
Clinical and Translational ReportCRISPR-Based Adenine Editors Correct Nonsense Mutations in a Cystic Fibrosis Organoid Biobank
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Graphical Abstract
Keywords
cystic fibrosis
genome editing
human intestinal organoids
patient-derived adult stem cells
organoid biobank
CRISPR/Cas9
adenine base-editing
CFTR mutations
evolved Cas9 proteins
Cas9 off-target analysis
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