Gene and cell therapy for cystic fibrosis: From bench to bedside
Under an Elsevier user license
open archive
Keywords
Cystic fibrosis
CFTR
Human artificial chromosome
Animal model
Vector development
Gene delivery
In utero gene therapy
Stem cells
Cited by (0)
- 1
Present address: Chromosome Medicine Procurement, Thérèse Studer Str. 47, 80797 Munich, Germany.
Copyright © 2011 European Cystic Fibrosis Society. Published by Elsevier B.V. All rights reserved.