Orphan diseases

Research priorities in alpha-1 antitrypsin deficiency (AATD) for healthcare professionals
Miriam Barrecheguren Fernandez, Maria Sucena, Karen O´hara, Marion Wilkens, Jeanette Boyd, Ewa Kolda, Alice Turner, Gerry Mcelvaney, Ilaria Ferrarotti, Jan Stolk, Joanna Chorostowska-Wynimko, Robert Stockley, Timm Greulich, Marc Miravitlles

European Respiratory Journal Sep 2020, 56 (suppl 64) 2430; DOI: 10.1183/13993003.congress-2020.2430
Oscillometry (OSC) to assess respiratory function in rare neuromuscular disease with respiratory muscle weakness (NMD)
Arash Rad, Marta Kaminska, Basil J. Petrof, Larry C. Lands, Zoltan Hantos, Ronald J. Dandurand, Stewart B. Gottfried

European Respiratory Journal Sep 2020, 56 (suppl 64) 1905; DOI: 10.1183/13993003.congress-2020.1905
Spontaneous resolutive pulmonary necrotizing granulomatosis
Bastien Weicker, Adeline Rosoux, Isabelle Gielen, Bruno Coulier, Richard Frognier

European Respiratory Journal Sep 2020, 56 (suppl 64) 1916; DOI: 10.1183/13993003.congress-2020.1916
Health state utilities in adult Primary Ciliary Dyskinesia patients
Panayiotis Kouis, Stavria Artemis Elia, Maria G. Kakkoura, Phivos Ioannou, Pinelopi Anagnostopoulou, Panayiotis K. Yiallouros

European Respiratory Journal Sep 2020, 56 (suppl 64) 1666; DOI: 10.1183/13993003.congress-2020.1666
Pirfenidone in unclassifiable ILD (uILD): subgroup analysis of patients with/without a surgical lung biopsy (SLB)
Vincent Cottin, Tamera J. Corte, Michael Kreuter, Maria Molina-Molina, Judit Axmann, Frank Gilberg, Klaus-Uwe Kirchgaessler, Toby M. Maher

European Respiratory Journal Sep 2020, 56 (suppl 64) 1802; DOI: 10.1183/13993003.congress-2020.1802
Long-term riociguat treatment towards implementing a targeted treatment strategy in patients with idiopathic pulmonary arterial hypertension
Anna Aleevskaya, Svetlana Gratsianskaya, Zarina Valieva, Tamila Martynyuk

European Respiratory Journal Sep 2020, 56 (suppl 64) 1465; DOI: 10.1183/13993003.congress-2020.1465
Zamicastat decreases cardiac arrhythmias in a rat model of pulmonary arterial hypertension
Nuno Pires, Bruno Igreja, Luis Magalhaes, Maria-Joao Bonifacio, Eric Chevalier, Patricio Soares-Da-Silva

European Respiratory Journal Sep 2020, 56 (suppl 64) 1483; DOI: 10.1183/13993003.congress-2020.1483
LTI-201: Evaluation of the hemodynamics and safety of inhaled LIQ861 (treprostinil) in pulmonary arterial hypertension (WHO Group 1) patients
Robert F. Roscigno, Marc Humbert, Toby Vaughn, Werner Seeger, Laurent Savale

European Respiratory Journal Sep 2020, 56 (suppl 64) 1459; DOI: 10.1183/13993003.congress-2020.1459
Drug-drug interaction study between zamicastat and sildenafil in healthy subjects
Ana Santos, João Ferreira, Helena Gama, Paulo Magalhães, Patricio Soares-Da-Silva

European Respiratory Journal Sep 2020, 56 (suppl 64) 1458; DOI: 10.1183/13993003.congress-2020.1458
Epidemiology of chronic thromboembolic pulmonary hypertension (CTEPH) in the Czech Republic
Pavel Jansa, David Ambrož, Matyáš Kuhn, Vladimír Dytrych, Aleš Linhart, Jaroslav Lindner, Audrey Muller

European Respiratory Journal Sep 2020, 56 (suppl 64) 1543; DOI: 10.1183/13993003.congress-2020.1543

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