Chronic ataluren (PTC124) treatment of nonsense mutation cystic fibrosis
M. Wilschanski, L.L. Miller, D. Shoseyov, H. Blau, J. Rivlin, M. Aviram, M. Cohen, S. Armoni, Y. Yaakov, T. Pugatch, M. Cohen-Cymberknoh, N.L. Miller, A. Reha, V.J. Northcutt, S. Hirawat, K. Donnelly, G.L. Elfring, T. Ajayi, E. Kerem
European Respiratory Journal Jul 2011, 38 (1) 59-69; DOI: 10.1183/09031936.00120910